10:00 AM – 11:00 AM Poster set up
12:00 PM – 1:00 PM Fireside Chat with Keynote
1:00 PM – 2:00 PM Poster Judging
2:00 PM – 3:00 PM Welcoming Remarks and Spotlight Speakers
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- Therapies for retinal degeneration: A new era with many lessons – Elise Héon, MD, FRCSC
- Hurdles of In vivo Systemic Gene transfer Therapy – Hernan Gonorazky, MD, CSCN Diplomate (EMG)
- Rare Disease Mother – Shillann Rodriguez- Pena
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3:00 PM – 4:00 PM Keynote
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- AADC deficiency – Krysztof Bankiewicz, MD, PhD
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4:00 PM – 5:30 PM Reception and Poster Awards